Increasing efficiency of preclinical research by group sequential designs
Journal article
Neumann, Konrad, Grittner, Ulrike, Piper, Sophie, Rex, Andre, Florez-Vargas, Oscar, Karystianis, George, Schneider, Alice, Wellwood, Ian, Siegerink, Bob, Ioannidis, John P. A., Kimmelman, Jonathan and Dirnagl, Ulrich. (2017). Increasing efficiency of preclinical research by group sequential designs. PLoS Biology. 15(3), p. Article e2001307. https://doi.org/10.1371/journal.pbio.2001307
Authors | Neumann, Konrad, Grittner, Ulrike, Piper, Sophie, Rex, Andre, Florez-Vargas, Oscar, Karystianis, George, Schneider, Alice, Wellwood, Ian, Siegerink, Bob, Ioannidis, John P. A., Kimmelman, Jonathan and Dirnagl, Ulrich |
---|---|
Abstract | Despite the potential benefits of sequential designs, studies evaluating treatments or experimental manipulations in preclinical experimental biomedicine almost exclusively use classical block designs. Our aim with this article is to bring the existing methodology of group sequential designs to the attention of researchers in the preclinical field and to clearly illustrate its potential utility. Group sequential designs can offer higher efficiency than traditional methods and are increasingly used in clinical trials. Using simulation of data, we demonstrate that group sequential designs have the potential to improve the efficiency of experimental studies, even when sample sizes are very small, as is currently prevalent in preclinical experimental biomedicine. When simulating data with a large effect size of d = 1 and a sample size of n = 18 per group, sequential frequentist analysis consumes in the long run only around 80% of the planned number of experimental units. In larger trials (n = 36 per group), additional stopping rules for futility lead to the saving of resources of up to 30% compared to block designs. We argue that these savings should be invested to increase sample sizes and hence power, since the currently underpowered experiments in preclinical biomedicine are a major threat to the value and predictiveness in this research domain. |
Year | 2017 |
Journal | PLoS Biology |
Journal citation | 15 (3), p. Article e2001307 |
Publisher | Public Library of Science |
ISSN | 1544-9173 |
Digital Object Identifier (DOI) | https://doi.org/10.1371/journal.pbio.2001307 |
PubMed ID | 28282371 |
Scopus EID | 2-s2.0-85016981067 |
PubMed Central ID | PMC5345756 |
Open access | Published as ‘gold’ (paid) open access |
Page range | 1-9 |
Funder | German Federal Ministry of Education and Research (BMBF) |
Publisher's version | License File Access Level Open |
Output status | Published |
Publication dates | |
Online | 10 Mar 2017 |
Publication process dates | |
Deposited | 02 Dec 2022 |
Grant ID | 01EO1301 |
https://acuresearchbank.acu.edu.au/item/8y829/increasing-efficiency-of-preclinical-research-by-group-sequential-designs
Download files
Publisher's version
OA_Neumann_2017_Increasing_efficiency_of_preclinical_research_by.pdf | |
License: CC BY 4.0 | |
File access level: Open |
49
total views27
total downloads1
views this month0
downloads this month